Hope, despair and CRISPR — the race to save one woman’s life

12 June 2024 Off By Bambam

Nature, Published online: 12 June 2024; doi:10.1038/d41586-024-01716-y

Researchers in India fought to develop what could have been the first therapy to use gene-editing to halt a rare neurodegenerative disease. The efforts hold lessons for the messy state of modern drug development.